Clinical Trial: Efficacy and Safety of IONIS-TTR Rx in Familial Amyloid Polyneuropathy

Study Status: Active, not recruiting
Recruit Status: Active, not recruiting
Study Type: Interventional




Official Title: A Phase 2/3 Randomized, Double-Blind, Placebo-Controlled Study to Assess the Efficacy and Safety of ISIS 420915 in Patients With Familial Amyloid Polyneuropathy

Brief Summary: The purpose of this study is to evaluate the efficacy and safety of IONIS-TTR Rx given for 65 weeks in patients with Familial Amyloid Polyneuropathy