Clinical Trial: Study of SOM0226 in Familial Amyloid Polyneuropathy

Study Status: Completed
Recruit Status: Completed
Study Type: Interventional




Official Title: Study of SOM0226 in Familial Amyloid Polyneuropathy (FAP) Patients and Asymptomatic Carriers to Evaluate Protein Stabilization Activity

Brief Summary: Clinical proof of concept study to evaluate SOM0226 efficacy in TTR Amyloidosis.