Clinical Trial: The Effect Of Tafamidis For The Transthyretin Amyloid Polyneuropathy Patients With V30M Or Non-V30M Transthyretin

Study Status: Completed
Recruit Status: Completed
Study Type: Interventional




Official Title: The Effect On Transthyretin Stabilization, Safety, Tolerablity, Efficacy And Pharmacokinetics Of Orally Administered Tafamidis In Transthyretin Amyloid Polyneuropathy Patients With V30m Or Non-v30m Tr

Brief Summary: Tafamidis has been developed as an oral specific stabilizer of transthyretin tetramer.