Clinical Trial: Study to Assess the Long Term Safety and Efficacy of UX007 in Subjects With Glucose Type 1 DS

Study Status: Enrolling by invitation
Recruit Status: Enrolling by invitation
Study Type: Interventional




Official Title: An Open-label Extension Study to Assess the Long-term Safety and Efficacy of UX007 in Subjects With Glucose Transporter Type 1 Deficiency Syndrome

Brief Summary: UX007G-CL202 is an open-label, single-arm, multi center extension study to assess the long-term safety and efficacy of UX007 in Glut 1 DS. The study will enroll up to 40 pediatric, adolescent and adult Glut 1 DS subjects who have completed the UX007G-CL201 study or participated in qualified ISTs.