Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional
Official Title: An Open-label Dose Escalation Study of an Adeno-associated Virus Vector (scAAV2-P1ND4v2) for Gene Therapy of Leber's Hereditary Optic Neuropathy (LHON) Caused by the G1177
Brief Summary:
Hypotheses:
The primary hypothesis being tested is that there will be no toxicity resulting in loss of vision to no light perception in injected eyes.