Clinical Trial: Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

Study Status: Completed
Recruit Status: Completed
Study Type: Interventional




Official Title: Investigation in the Pathogenesis of Liver Disease in Patients With Inborn Errors of Bile Acid Metabolism." This Study Was Previously Registered by the NCRR and Identified as NCRR-M01RR08084-0009

Brief Summary:

OBJECTIVES:

I. To Evaluate the therapeutic efficacy of cholic acid during provision of compassionate treatment to patients with identified inborn errors of bile acid synthesis and metabolism

II. To assess the safety and tolerability of cholic acid