Study Name: Clinical Study of a Single Ciliopathy: Alström Syndrome
Condition: Alström Syndrome (ALMS)
Study Name: Safety and Tolerability of PBI-4050 and Its Effects on the Biomarkers in Subjects With Alström Syndrome
Interventions: Drug: PBI-4050
Four 200 mg capsules (800 mg total) administered orally, once daily.
Study Name: Setmelanotide Phase 2 Treatment Trial in Patients With Rare Genetic Disorders of Obesity|