Status | Study |
Not yet recruiting |
Study Name: Pharmacokinetics, Pharmacodynamics And Safety Study Of Elelyso(tm) In Pediatric Subjects With Type 1 Gaucher Disease Condition: Type 1 Gaucher Disease Date: 2016-09-23 Interventions: Drug: Elelyso 60 units/kg All patients receive Elelyso 60 units/kg. |
Recruiting |
Study Name: GZ/SAR402671 in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 Condition: Gaucher Disease Type 1-Gaucher Disease Type 3 Date: 2016-07-20 Interventions: Drug: GZ402671 Other Name: Venglustat |
Completed |
Study Name: Safety and Efficacy of ISU302 in Patients With Type 1 Gaucher Disease Condition: Gaucher Disease, Type 1 Date: 2016-05-07 Interventions: Drug: ISU302 60 U/kg given intravenously Other Name: |
Recruiting |
Study Name: Phase 4 Study to Evaluate the Effect of Velaglucerase Alfa (VPRIV®) on Patients With Type 1 Gaucher Disease Through the IV Administration of VPRIV® Over 2 Years Condition: Gaucher Disease Date: 2015-10-09 Interventions: Drug: Velaglucerase alfa VPRIV |
Recruiting |
Study Name: Role of Oxidative Stress and Inflammation in Type 1 Gaucher Disease (GD1) Condition: Gaucher Disease Type 1 Date: 2015-08-21 Interventions: Drug: N-acetylcysteine 1800mg NAC twice daily (3600mg/day) orally for approximately 90 days. |
Recruiting |
Study Name: The Effect of Velaglucerase Alfa (Vpriv) on Skeletal Development in Pediatric Gaucher Disease Condition: Gaucher Disease Type 1 Gaucher Disease Type 3 Date: 2015-07-28 Interventions: Drug: Velaglucerase alfa Enzyme replacement therapy |
Recruiting |
Study Name: Oxidative Stress-Related Biomarkers in Gaucher Disease: A Preliminary Study Condition: Gaucher Disease Type I Oxidative Stress Date: 2015-05-04 |
Completed |
Study Name: Comparison of BMD Measurement by DEXA to BeamMed Speed-of-Sound Measurement at Forearm in Patients With Gaucher Disease Condition: Gaucher Disease Type 1 Date: 2014-01-27 Interventions: Device: BeamMed Speed-of-Sound bone strength test at forearm BeamMed Speed-of-Sound bone strength test a |
Completed |
Study Name: A Switch-Over Study of the Safety and Efficacy of ISU302 in Patients With Type 1 Gaucher Disease Condition: Gaucher Disease Date: 2014-01-26 |
Completed |
Study Name: Validating a New Severity Score System for Adults With Type 1 Gaucher Disease (GD1) Condition: Gaucher Disease Date: 2010-05-31 Interventions: Drug: Imiglucerase Imiglucerase intravenous infusions regardless of dose or schedule of administration. |