Status | Study |
Recruiting |
Study Name: A Trial of PF-06252616 in Ambulatory Participants With LGMD2I Condition: LGMD2I Date: 2016-07-12 Interventions: Drug: PF 06252616 |
Completed |
Study Name: MRI on Persons With Mutations in POMT2 Gene (LGMD2N) Condition: Limb-girdle Muscular Dystrophy Date: 2016-04-27 |
Recruiting |
Study Name: rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies Condition: Dysferlinopathy Date: 2016-02-11 Interventions: Drug: rAAVrh74.MHCK7.DYSF.DV Biological/Vaccine: rAAVrh74.MHCK7.DYSF.DV Recombinant adeno-associated vir |
Completed |
Study Name: The Safety and Biological Activity of ATYR1940 in Patients With Limb Girdle or Facioscapulohumeral Muscular Dystrophies Condition: Limb-Girdle Muscular Dystrophies Facioscapulohumeral Muscular Dystrophy Date: 2015-09-28 Interventions: Biological: ATYR1940 Intrapati |
Completed |
Study Name: Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I Condition: Becker Muscular Dystrophy Limb-Girdle Muscular Dystrophy Type 2 Date: 2014-06-11 |
Enrolling by invitation |
Study Name: Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA Condition: Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) Date: 2013-07-24 Interventions: Drug: scAAVrh74.tMCK.hSGCA |
Active, not recruiting |
Study Name: Clinical Outcome Study for Dysferlinopathy Condition: Dysferlinopathy LGMD2B Miyosh Date: 2012-08-28 |
Recruiting |
Study Name: Congenital Muscle Disease Study of Patient and Family Reported Medical Information Condition: Congenital Muscular Dystrophy (Including Unspecified/Undiagnosed) Dystroglycanopathy Date: 2011-07-26 |
Completed |
Study Name: Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C Condition: Limb Girdle Muscular Dystrophy Type 2C Gamma-sarcoglycanopathy Date: 2011-03-17 Interventions: Biological: AAV1-gamma-sarcoglycan vector injection single intramuscular injection into carpi radialis m |
Completed |
Study Name: Deflazacort in Dysferlinopathies Condition: LGMD2B Miyoshi Myopathy Dysfe Date: 2007-09-06 Interventions: Drug: deflazacort In the first |