Status | Study |
Recruiting |
Study Name: Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome Condition: Mucopolysaccharidosis II Date: 2014-10-02 Interventions: Drug: AGT-182 Recombinant HIRMAb-IDS |
No longer available |
Study Name: An Open-Label Treatment Protocol With UX003 rhGUS Enzyme Replacement Therapy for an Advanced Stage MPS 7 Patient Condition: Mucopolysaccharidosis Type 7 Date: 2014-03-24 Interventions: Drug: UX003 Open Label Other Names: |
Completed |
Study Name: Natural History Studies of Mucopolysaccharidosis III Condition: Mucopolysaccharidosis Type IIIA Mucopolys Date: 2013-11-26 Interventions: Procedure: Lumbar puncture Device: Magneti |
Completed |
Study Name: An Open-Label Phase 1/2 Study to Assess the Safety, Efficacy and Dose of Study Drug UX003 Recombinant Human Beta-glucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With MPS 7 Condition: Mucopolysaccharidosis Type 7 Date: 2013-05-08 Interventions: Drug: UX003 |
Terminated |
Study Name: Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA Condition: Mucopolysaccharidosis Type IVA Date: 2012-11-21 |
Completed |
Study Name: Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease Condition: Mucopolysaccharidosis IV A Mucopolysaccha Date: 2012-10-12 Interventions: Other: Enzyme testing Leukocyte activity measurement of Arylsulfatase B and N acetyl galactosamine 6 sul |
Active, not recruiting |
Study Name: Longitudinal Study of Bone Disease in Children With Mucopolysaccharidoses (MPS) I, II, and VI Condition: Mucopolysaccharidoses Date: 2011-11-11 |
Completed |
Study Name: To Evaluate the Safety and Efficacy of GC1111 (Recombinant Human Iduronate-2-sulfatase) in Hunter Syndrome Patients Condition: Mucopolysaccharidosis II Date: 2011-02-22 Interventions: Drug: GC1111_0.5mg/kg Drug: GC1111_1.0mg/k |
Recruiting |
Study Name: Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis Condition: Mucopolysaccharidosis Date: 2010-11-08 Interventions: Drug: Conditioning regimen |
Completed |
Study Name: Immune Tolerance Study With Aldurazyme® (Laronidase) Condition: Mucopolysaccharidosis I Date: 2008-08-13 Interventions: Biological: Laronidase 0.058 m |