Status | Study |
Recruiting |
Study Name: Use of ACTIMMUNE in Patients With ADO2 Condition: Autosomal Dominant Osteopetrosis Type 2 Date: 2015-10-20 Interventions: Drug: ACTIMMUNE |
Recruiting |
Study Name: ACTIMMUNE in Intermediate Osteopetrosis Condition: Osteopetrosis Date: 2015-06-23 Interventions: Drug: Interferon gamma-1b gamma interferon-1b dose escalation over first 4 weeks of study to 100 mcg SC |
Recruiting |
Study Name: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Condition: Mucopolysaccharidosis Disorders Hurler Syndrome Hunter Syn Date: 2014-06-20 Interventions: Biological: Stem Cell Transplantation |
Recruiting |
Study Name: Reduced Intensity Conditioning in Patients Aged ≤35 With Non-Malignant Disorders Undergoing UCBT, BMT, or PBSCT Condition: Primary Immunodeficiency Syndromes Congenital Bone Marrow Failure Syndromes Date: 2013-10-10 Interventions: Drug: Hydroxyurea Hydroxyurea |
Completed |
Study Name: Clinical Assessment of Patients With High Bone Mass Due to Mutation in Lrp5 Condition: Osteopetrosis Date: 2010-09-09 |
Available |
Study Name: Expanded Access Protocol (EAP) Using the CliniMACS® Device for Pediatric Haplocompatible Donor Stem Cell Transplant Condition: Acute Lymphoblastic Leukemia Acute Myeloid Leukemia Chroni Date: 2010-09-09 Interventions: Biological: CD34+ enriched, T Cell Depleted donor stem cell product stem cell transplant |
Terminated |
Study Name: Hematopoietic Stem Cell Transplantation for Malignant Infantile Osteopetrosis Condition: Osteopetrosis Date: 2010-03-13 Interventions: Drug: Busulfan, Cyclophosphamide, Thymoglobulin, Fludarabine (Conditioning r |
Recruiting |
Study Name: Risk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant Diseases Condition: Bone Marrow Failure Osteopetrosis Date: 2009-11-23 Interventions: Drug: Fludarabine Fludarabine/ |
Terminated |
Study Name: T-cell Depleted Alternative Donor Transplantation Condition: Acute Lymphoblastic Leukemia Acute Myeloid Leukemia Chroni Date: 2009-08-28 Interventions: Device: CliniMACS® (T cell depletion) Stem cells will be collected from donors after they receive G |
Terminated |
Study Name: Allogeneic Transplantation For Severe Osteopetrosis Condition: Severe Osteopetrosis Date: 2008-10-16 Interventions: Procedure: umbilical cord blood transplantation |