Status | Study |
Recruiting |
Study Name: Autologous Cryopreserved CD34+ Hematopoietic Cells Transduced With EFS-ADA Lentivirus for ADA SCID Condition: Severe Combined Immunodeficiency Due to ADA Deficiency Date: 2016-12-19 Interventions: Biological: Infusion of autologous cryopreserved EFS-ADA LV CD34+ cells Infusion of OTL-101 after reduce |
Not yet recruiting |
Study Name: Safety and Early Efficacy Study of TBX-1400 in Patients With Severe Combined Immunodeficiencies Condition: Severe Combined Immunodeficiency Date: 2016-07-26 Interventions: Biological: TBX-1400 |
Recruiting |
Study Name: Neonatal Screening of Severe Combined Immunodeficiencies Condition: Severe Combined Immunodeficiency Neonatal Screening Date: 2015-10-27 |
Active, not recruiting |
Study Name: Generalized Neonatal Screening of Severe Combined Immunodeficiencies Condition: Severe Combined Immunodeficiency, Atypical Date: 2014-09-02 Interventions: Biological: SCID screening |
Active, not recruiting |
Study Name: Clinical Characteristics and Genetic Profiles of Severe Combined Immunodeficiency in China Condition: Severe Combined Immunodeficiency Date: 2014-09-01 Interventions: Genetic: gene sequencing Amplify and identify exons from gene IL-2RG by PCR and agarose gel electrophore |
Enrolling by invitation |
Study Name: SCID Bu/Flu/ATG Study With T Cell Depletion Condition: Severe Combined Immunodeficiency Date: 2012-10-19 Interventions: Biological: unrelated BM with T cell depletion |
Recruiting |
Study Name: Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants Condition: Severe Combined Immunodeficiency Disease, X-linked Date: 2012-01-13 Interventions: Genetic: CL20-4i-EF/a-hyc-OPT |
Active, not recruiting |
Study Name: Gene Therapy for X-linked Severe Combined Immunodeficiency Condition: X-linked Severe Combined Immunodeficiency Date: 2011-06-21 Interventions: Other: Gene transfer Single infusion of autologous CD34+ cells transduced with the self-inactivating (SI |
Recruiting |
Study Name: Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID) Condition: X-linked Severe Combined Immunodeficiency XSCID Date: 2011-02-26 Interventions: Other: Gene-modified CD34+ Hematopoietic stem cells |
Terminated |
Study Name: Hematopoietic Stem Cell Transplantation (HSCT) for Children With SCID Utilizing Alemtuzumab, Plerixafor & Filgrastim Condition: Severe Combined Immunodeficiency Date: 2010-08-09 Interventions: Drug: Transplant Conditioning with Mobilization Only |