Clinical Trial: Gene Therapy ADA Deficiency

Study Status: Completed
Recruit Status: Completed
Study Type: Interventional




Official Title: Phase I Gene Therapy Protocol for Adenosine Deaminase Deficiency

Brief Summary: Adenosine deaminase deficiency is an inherited disorder that results in severe abnormalities of the immune system and leaves children unable to fight infection. This trial aims to treat adenosine deaminase deficiency patients using gene therapy.