Clinical Trial: Stem Cell Transplant for Inborn Errors of Metabolism

Study Status: Completed
Recruit Status: Completed
Study Type: Interventional




Official Title: Treatment of Lysosomal and Peroxisomal Inborn Errors of Metabolism by Bone Marrow Transplantation

Brief Summary: The purpose of this study is to determine the safety and engraftment of donor hematopoietic cells using this conditioning regimen in patients undergoing a hematopoietic (blood forming) cell transplant for an inherited metabolic storage disease.