Study Status: NOT_YET_RECRUITING
Recruit Status: NOT_YET_RECRUITING
Study Type: OBSERVATIONAL
Official Title: Liver Biopsy Following Gene Therapy For Hemophilia
Brief Summary: This observational study will obtain liver biopsy samples and evaluate the long-term effect of adeno-associated virus (AAV)-mediated gene therapy on the liver tissue in adult patients with hemophilia A or hemophilia B who have previously been treated with a factor VIII or factor IX gene-containing AAV-vector for liver-targeted gene transfer.
Participants are from a cohort of patients treated with AAV-mediated gene transfer and at least 6 months after vector infusion