Clinical Trial: An Observational Cohort Study to Characterize the Effectiveness and Safety of HEMGENIX� in Patients With Hemophilia B

Study Status: RECRUITING
Recruit Status: RECRUITING
Study Type: OBSERVATIONAL




Official Title: An Observational Post-authorization Long-term Follow-up Study to Characterize the Effectiveness and Safety of HEMGENIX� (Etranacogene Dezaparvovec) in Patients With Hemophilia B

Brief Summary: This observational, post-authorization, long-term follow-up study aims to investigate the short and long-term effectiveness and safety of HEMGENIX in patients with hemophilia B. The study will also include a cohort of patients with hemophilia B treated with FIX prophylaxis to enable interpretation of relevant efficacy and safety findings of HEMGENIX.