Clinical Trial: Immune Modulation Therapy for Pompe Disease

Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional




Official Title: Immune Modulation Therapy for ERT-naïve or ERT-treated Pompe Disease Patients

Brief Summary: The purpose of this study is to assess anti-recombinant human acid α-glucosidase (anti-rhGAA) antibody titers after treatment with immune modulation therapy in patients of Pompe disease.