Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional
Official Title: An Open-Label, Multicenter, Multinational Extension Study Of The Long-Term Safety And Pharmacokinetics Of Repeated Biweekly Infusions Of NeoGAA In Patients With Pompe Disease
Brief Summary:
Primary Objective:
Long-term safety and pharmacokinetics (PK) of neoGAA
Secondary Objective:
Long-term effect of neo-GAA on pharmacodynamic and exploratory efficacy variables