Clinical Trial: A Gene Therapy Study for Hemophilia B

Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional




Official Title: Gene Therapy, Open-label, Dose-escalation Study of SPK-9001 [Adeno-associated Viral Vector With Human Factor IX Gene] in Subjects With Hemophilia B

Brief Summary: A Phase 1/2, Open-Label, Non-Randomized, Dose-Escalation Study of SPK-9001 in Subjects with Hemophilia B.