Clinical Trial: A Study of ALN-PCSSC in Participants With Homozygous Familial Hypercholesterolemia

Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional




Official Title: An Open-Label, Single-Arm, Multicenter Pilot Study to Evaluate Safety, Tolerability, and Efficacy of ALN-PCSSC in Subjects With Homozygous Familial Hypercholesterolemia

Brief Summary: The purpose of this study is to assess the safety, tolerability, and efficacy of ALN-PCSSC in participants with homozygous familial hypercholesterolemia.