Clinical Trial: A Long-Term Extension Study of RP103-MITO-001 (NCT02023866) to Assess RP103 in Children With Inherited Mitochondrial Disease

Study Status: Completed
Recruit Status: Completed
Study Type: Interventional




Official Title: A Long-Term Open-Label Extension Study of RP103-MITO-001 to Assess the Safety, Tolerability and Efficacy of Cysteamine Bitartrate Delayed-release Capsules (RP103) for Treatment of Children With Inheri

Brief Summary: A long-term extension study of patients with mitochondrial diseases, who are ≥ 6 years old and < 18 years previously enrolled into the RP103-MITO-001 (NCT02023866) study assessing the safety, tolerability and efficacy of RP103.