Clinical Trial: Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome

Study Status: Enrolling by invitation
Recruit Status: Enrolling by invitation
Study Type: Interventional




Official Title: EPI743-13-023: Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome

Brief Summary: EPI-743 in Leigh syndrome subjects that participated in previous EPI743-12-002 study.