Clinical Trial: Study of Tideglusib in Adolescent and Adult Patients With Myotonic Dystrophy

Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional




Official Title: A Single-Blind, Phase 2 Study To Evaluate The Safety And Efficacy Of Tideglusib 400mg Or 1000mg For The Treatment Of Adolescent And Adult Congenital And Juvenile-Onset Myotonic Dystrophy

Brief Summary: The purpose of this study is to determine whether Tideglusib is safe and efficacious in the treatment of adolescents and adults with congenital and juvenile-onset Myotonic Dystrophy. The pharmacokinetics of tideglusib and its primary metabolite will also be investigated.