Clinical Trial: ACTIMMUNE in Intermediate Osteopetrosis

Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional




Official Title: Open-label Early Phase 2 Study With a Single Arm of Interferon Gamma-1b Treatment of Osteopetrosis

Brief Summary: This study evaluates the effects of ACTIMMUNE (IFN-γ1b) in children and adults with intermediate osteoporosis. All participants will receive treatment with ACTIMMUNE for 12 months. The investigators hypothesize that ACTIMMUNE will be tolerated by participants for the full 12 months and result in decreased disease severity.