Status | Study |
NOT_YET_RECRUITING |
Study Name: Open Label Extension Study of INBRX-101 in Adults With AATD Emphysema Condition: Date: 2023-05-31 Interventions: A1PI, Recombinant, Bivalent Fc Fusion Protein |
Recruiting |
Study Name: The Impact of Delayed Diagnosis of Alpha-1 Antitrypsin Deficiency Condition: Alpha 1-Antitrypsin Deficiency Date: 2017-01-31 |
Recruiting |
Study Name: Targeting Pulmonary Perfusion in Alpha-1 Antitrypsin Deficiency Condition: Alpha-1 Antitrypsin Deficiency Emphysema Date: 2016-12-22 Interventions: Drug: Aspirin 81mg aspirin tak |
Recruiting |
Study Name: Liver Disease in Patients With alpha1-antitrypsin Deficiency Condition: alpha1-antitrypsin Deficiency Date: 2016-10-06 Interventions: Other: No intervention No Intervention, observational |
Not yet recruiting |
Study Name: Effects of Pulmonary Rehabilitation on Skeletal Muscle in COPD Patients Condition: Chronic Obstructive Pulmonary Disease Date: 2016-09-21 Interventions: Procedure: Pulmonary rehabilitation 3-weeks of inpatient pulmonary Rehabilitation including exercise Tra |
Enrolling by invitation |
Study Name: FibroScan™ in Pediatric Cholestatic Liver Disease Study Protocol Condition: Biliary Atresia Alagille Syndrome Al Date: 2016-09-20 Interventions: Other: Liver Stiffness Measurement (LSM) LSM will be measured via transient elastography utilizing the n |
Withdrawn |
Study Name: Safety, Tolerability and Effect of ARC-AAT Injection on Circulating and Intrahepatic Alpha-1 Antitrypsin Levels Condition: Alpha-1 Antitrypsin Deficiency Date: 2016-09-09 Interventions: Drug: ARC-AAT Injection RNA interference (RNAi)-based, liver-targeted therapeutic |
Recruiting |
Study Name: Safety and Pharmacokinetics of Alpha-1 MP in Patients With Alpha1-Antitrypsin Deficiency Condition: Alpha1-Antitrypsin Deficiency Date: 2016-08-12 Interventions: Biological: Alpha-1 MP Alpha-1 MP is a stable, sterile, lyophilized preparation of human alpha1-PI, also |
Enrolling by invitation |
Study Name: Long-term Safety of Alpha1-Proteinase Inhibitor (Human) in Japanese Subjects With Alpha1 Antitrypsin Deficiency (GTI1401-OLE) Condition: Alpha1-Antitrypsin Deficiency Date: 2016-08-12 Interventions: Biological: Alpha-1 MP Weekly intravenous infusions of 60 mg/kg Alpha-1 MP |
Completed |
Study Name: Alpha-1 Carrier Genomics Study Condition: Alpha-1 Antitrypsin Deficiency Emphysema Date: 2016-06-20 Interventions: Genetic: Genetic Sequencing Sequencing of the SERPINA1 gene |