| Status | Study |
| Recruiting |
Study Name: Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A Condition: Fanconi Anemia Date: 2017-04-26 Interventions: Procedure: IV administration of Genetically Engineered Hematopoietic Stem/Pr |
| Not yet recruiting |
Study Name: Patient-Driven Transfusion Thresholds in Hematological Disorders: A Pilot Study Condition: Anemia Aplastic Anemia Bone M Date: 2017-03-17 Interventions: Procedure: Red Blood Cell Transfusions (RBCT) Undergo patient-driven RBCT |
| Recruiting |
Study Name: Familial Investigations of Childhood Cancer Predisposition Condition: Acute Leukemia Adenomatous Polyposis Adrenocortical Carcin Date: 2017-02-08 |
| Recruiting |
Study Name: Unrelated And Partially Matched Related Donor PSCT w/ TCR αβ Depletion for Patients With BMF Condition: Acquired Aplastic Anemia Paroxysmal Nocturnal Hemoglobinuria Date: 2017-02-07 Interventions: Device: CliniMACs Peripheral blood stem cells from closely matched unrelated or partially matched relate |
| Recruiting |
Study Name: Umbilical Cord Derived Mesenchymal Stem Cells Therapy in Aplastic Anemia Condition: Aplastic Anemia Date: 2017-02-04 Interventions: Biological: mesenchymal stem cells Patients in the cell treated group were given umbilical cord derived |
| Not yet recruiting |
Study Name: A Phase II Dose-escalation Study Characterizing the PK of Eltrombopag in Pediatric Patients With Previously Untreated or Relapsed Severe Aplastic Anemia or Recurrent Aplastic Anemia Condition: Aplastic Anemia Date: 2017-01-12 Interventions: Drug: Eltrombopag Tablet for o |
| Recruiting |
Study Name: Combined Cord Blood Transplant Condition: Acute Leukemia Immune Deficiency Disorder Congenital Hemat Date: 2016-12-26 Interventions: Radiation: Total Body Irradiation 1200 cGy |
| Recruiting |
Study Name: Sirolimus (Rapamune ) for Relapse Prevention in People With Severe Aplastic Anemia Responsive to Immunosuppressive Therapy Condition: Severe Aplastic Anemia Date: 2016-12-01 Interventions: Drug: Sirolimus Sirolimus will be started on day 1 for subjects in the Sirolimus arm. A baseline CBC wil |
| Recruiting |
Study Name: Clinical Trial Using an Engineered Peripheral Blood Graft for Haploidentical Transplantation Condition: Leukemia Date: 2016-11-08 Interventions: Drug: Rituximab CD20 positive |
| Not yet recruiting |
Study Name: Eltrombopag Combined With Cyclosporine as First Line Therapy in Patients With Severe Acquired Aplastic Anemia Condition: Severe Aplastic Anemia Date: 2016-11-04 Interventions: Drug: eltrombopag Film-coated |