Status | Study |
Not yet recruiting |
Study Name: Adiponectin, IL-6 and hsC-RP in Relation to Carotid Intima-media Thickness in B-thalassemia Patients Condition: Thalassemia Date: 2017-05-26 Interventions: Diagnostic Test: Interleukin-6 |
Not yet recruiting |
Study Name: Examining the Knowledge, Attitudes, and Beliefs of Sickle Cell Disease Patients, Parents of Patients With Sickle Cell Disease, and Providers Towards the Integration of CRISPR in Clinical Care Condition: Sickle Cell Disease Date: 2017-05-24 |
Not yet recruiting |
Study Name: Evaluation of Nutritional Status in Thalassemia Major Patients in Assiut Children Hospital Condition: Thalassemia Major Date: 2017-05-19 |
Recruiting |
Study Name: Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ISIS 702843 Administered Subcutaneously to Healthy Volunteers Condition: Thalassemia Date: 2017-05-18 Interventions: Drug: IONIS TMPRSS6-Lrx Ascend |
Not yet recruiting |
Study Name: Sleep and Pain in Sickle Cell Disease Condition: Sickle Cell Disease Sleep Disturbance Pain Date: 2017-05-03 Interventions: Behavioral: Behavioral symptom management |
Not yet recruiting |
Study Name: A Study to Evaluate Safety, Pharmacokinetic, and Biological Activity of INCB059872 in Subjects With Sickle Cell Disease Condition: Sickle Cell Disease Date: 2017-04-24 Interventions: Drug: INCB059872 INCB059872 at the protocol-defined dose administered QOD or QD based on cohort assignme |
Recruiting |
Study Name: A Study to Compare if the Uptake of Ticagrelor in the Body Differs When Different Tablets Are Administered Condition: Sickle Cell Disease Date: 2017-04-20 Interventions: Drug: Ticagrelor granule A P2Y |
Recruiting |
Study Name: Haploidentical Hematopoietic Stem Cell Transplantation for Patients With Thalassemia Major Condition: Thalassemia Major Date: 2017-04-18 Interventions: Drug: Busulfan Busulfan( |
Not yet recruiting |
Study Name: Erythrocyte Glutamine/Glutamate Ratio Relation to Pulmonary Hypertension Risk in Thalassemic Children Condition: Thalassemia in Children Pulmonary Hypertension Hemolysis Date: 2017-04-15 Interventions: Diagnostic Test: Erythrocyte glutamine/glutamate ratio |
Recruiting |
Study Name: Study of HLA-Haploidentical Stem Cell Transplantation to Treat Clinically Aggressive Sickle Cell Disease Condition: Sickle Cell Disease Date: 2017-04-14 Interventions: Drug: ATG 0.5 mg/kg IV on day |