| Status | Study |
| Recruiting |
Study Name: A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion Condition: Aromatic Amino Acid Decarboxylase Deficiency Date: 2016-10-03 Interventions: Drug: AAV2-hAADC Dosage form: Aqueous solutionDose(s): 2.371x1011 vg/case Dosing schedule: Intracerebral |
| Recruiting |
Study Name: A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients Condition: AADC Deficiency Date: 2016-07-20 Interventions: Drug: AAV2-hAADC Subjects will be enrolled sequentially in |
| Completed |
Study Name: Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency Condition: Aromatic L-amino Acid Decarboxylase Deficiency Date: 2015-03-21 |
| Completed |
Study Name: A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC Condition: Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Date: 2011-06-12 Interventions: Drug: gene therapy AAV2-hAADC viral vector will be injected into bilateral putamen by stereotactic surge |