Status | Study |
Not yet recruiting |
Study Name: Study of Olaparib/Trabectedin vs. Doctor's Choice in Solid Tumors Condition: Cancers With DNA Repair-Deficiency Date: 2017-03-31 Interventions: Drug: Olaparib Olaparib 150 mg |
Recruiting |
Study Name: Autologous Cryopreserved CD34+ Hematopoietic Cells Transduced With EFS-ADA Lentivirus for ADA SCID Condition: Severe Combined Immunodeficiency Due to ADA Deficiency Date: 2016-12-19 Interventions: Biological: Infusion of autologous cryopreserved EFS-ADA LV CD34+ cells Infusion of OTL-101 after reduce |
Recruiting |
Study Name: Docetaxel and Carboplatin for Patients With mCRPC and DNA-Repair Deficiencies Condition: Hormone-Resistant Prostate Cancer Metastatic Prostate Carcinoma Date: 2016-11-22 Interventions: Drug: Carboplatin Chemotherapy |
Not yet recruiting |
Study Name: Safety and Early Efficacy Study of TBX-1400 in Patients With Severe Combined Immunodeficiencies Condition: Severe Combined Immunodeficiency Date: 2016-07-26 Interventions: Biological: TBX-1400 |
Recruiting |
Study Name: Neonatal Screening of Severe Combined Immunodeficiencies Condition: Severe Combined Immunodeficiency Neonatal Screening Date: 2015-10-27 |
Active, not recruiting |
Study Name: Generalized Neonatal Screening of Severe Combined Immunodeficiencies Condition: Severe Combined Immunodeficiency, Atypical Date: 2014-09-02 Interventions: Biological: SCID screening |
Active, not recruiting |
Study Name: Clinical Characteristics and Genetic Profiles of Severe Combined Immunodeficiency in China Condition: Severe Combined Immunodeficiency Date: 2014-09-01 Interventions: Genetic: gene sequencing Amplify and identify exons from gene IL-2RG by PCR and agarose gel electrophore |
Withdrawn |
Study Name: Sirolimus Prophylaxis for aGVHD in TME SCID Condition: Severe Combined Immunodeficiency Transplacental Maternal Engraftment Date: 2014-06-19 Interventions: Drug: Sirolimus Other Name: Rapamune |
Recruiting |
Study Name: Study to Determine and Evaluate a Safe and Tolerated Dose of HDM201 in Patients With Selected Advanced Tumors That Are TP53wt Condition: Advanced Solid and Hematological TP53wt Tumors Date: 2014-05-19 Interventions: Drug: HDM201 Drug: ancillary treatment |
Active, not recruiting |
Study Name: Autologous Transplant of EFS-ADA Modified Bone Marrow Cells for ADA-Deficient Severe Combined Immunodeficiency (SCID) Condition: ADA-SCID Date: 2013-05-07 Interventions: Genetic: EFS-ADA transduced CD34+ cells from the bone marrow Eligible subjects will undergo bone marrow |