Status | Study |
Recruiting |
Study Name: rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies Condition: Dysferlinopathy Date: 2016-02-11 Interventions: Drug: rAAVrh74.MHCK7.DYSF.DV Biological/Vaccine: rAAVrh74.MHCK7.DYSF.DV Recombinant adeno-associated vir |
Recruiting |
Study Name: Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin Condition: Dysferlinopathy Date: 2013-04-29 Interventions: Drug: Bortezomib Other Name: Velcade® |
Active, not recruiting |
Study Name: Clinical Outcome Study for Dysferlinopathy Condition: Dysferlinopathy LGMD2B Miyosh Date: 2012-08-28 |
Completed |
Study Name: Deflazacort in Dysferlinopathies Condition: LGMD2B Miyoshi Myopathy Dysferlinopa Date: 2007-09-06 Interventions: Drug: deflazacort In the first |