Status | Study |
Recruiting |
Study Name: Biomarker for Mucolipidosis Disorder Type I, II, III or IV Condition: Mucolipidosis Type I Mucolipidosis Type II Date: 2014-10-23 |
Completed |
Study Name: Longitudinal Studies of the Glycoproteinoses Condition: Aspartylglucosaminuria Fucosidosis Galactosialidosis Date: 2013-05-22 |
Completed |
Study Name: Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders Condition: Lysosomal Storage Disease Peroxisomal Disorder Date: 2012-06-20 Interventions: Drug: Campath-1H A daily dose |
Terminated |
Study Name: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases Condition: Inherited Metabolic Diseases Lysosomal Storage Disorders P Date: 2008-04-03 Interventions: Biological: ALD-101 A subpopulation of cord blood cells composed of cells that express a high level of t |
Completed |
Study Name: HSCT for High Risk Inherited Inborn Errors Condition: Adrenoleukodystrophy Metachromatic Leukodystrophy Globoid Date: 2006-09-29 Interventions: Drug: Clofarabine days -7 thro |
Completed |
Study Name: Stem Cell Transplantation for Hurler Condition: Mucopolysaccharidosis I Mucopolysaccharidosis VI Mannosido Date: 2005-09-12 Interventions: Procedure: Stem Cell Transplant |
Completed |
Study Name: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation Condition: I Cell Disease Fucosidosis Gl Date: 2000-06-02 |