Status | Study |
Recruiting |
Study Name: rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies Condition: Dysferlinopathy Date: 2016-02-11 Interventions: Drug: rAAVrh74.MHCK7.DYSF.DV Biological/Vaccine: rAAVrh74.MHCK7.DYSF.DV Recombinant adeno-associated vir |
Completed |
Study Name: The Safety and Biological Activity of ATYR1940 in Patients With Limb Girdle or Facioscapulohumeral Muscular Dystrophies Condition: Limb-Girdle Muscular Dystrophies Facioscapulohumeral Muscular Dystrophy Date: 2015-09-28 Interventions: Biological: ATYR1940 Intrapati |
Active, not recruiting |
Study Name: Clinical Outcome Study for Dysferlinopathy Condition: Dysferlinopathy LGMD2B Miyosh Date: 2012-08-28 |
Completed |
Study Name: Evaluation of Limb-Girdle Muscular Dystrophy Condition: Becker Muscular Dystrophy Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) Date: 2009-05-04 |
Completed |
Study Name: Deflazacort in Dysferlinopathies Condition: LGMD2B Miyoshi Myopathy Dysfe Date: 2007-09-06 Interventions: Drug: deflazacort In the first |