Status | Study |
Recruiting |
Study Name: Safety and Efficacy Study of Gene Therapy for The Treatment of Leber's Hereditary Optic Neuropathy Condition: Leber Hereditary Optic Neuropathy Date: 2017-05-10 Interventions: Drug: rAAV2-ND4 a Single IVT I |
Recruiting |
Study Name: Stem Cell Ophthalmology Treatment Study II Condition: Retinal Disease Age-Related Macular Degeneration Retinitis Date: 2017-01-01 Interventions: Procedure: Arm 1 |
Not yet recruiting |
Study Name: Treatment of Wolfram Syndrome Type 2 With the Chelator Deferiprone and Incretin Based Therapy Condition: Diabetes Mellitus Iron Metabolism Disorders Gastroduodenal Date: 2016-07-17 Interventions: Drug: Deferiprone Other Name: |
Recruiting |
Study Name: Wolfram Syndrome International Registry and Clinical Study Condition: Wolfram Syndrome Diabetes Mellitus Optic Nerve Atrophy Date: 2016-07-06 |
Recruiting |
Study Name: A Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome Condition: Wolfram Syndrome Diabetes Mellitus Optic Nerve Atrophy Date: 2016-07-06 Interventions: Drug: dantrolene sodium The purpose of this study is to as |
Recruiting |
Study Name: Historical Case Record Survey of Visual Acuity Data From Patients With Leber's Hereditary Optic Neuropathy (LHON) Condition: Leber's Hereditary Optic Neuropathy (LHON) Date: 2016-06-07 |
Recruiting |
Study Name: Study to Assess the Efficacy and Safety of Raxone in LHON Patients Condition: Leber's Hereditary Optic Neuropathy (LHON) Date: 2016-05-12 Interventions: Drug: Idebenone Other Name: Raxone |
Recruiting |
Study Name: Post Authorisation Safety Study With Raxone in LHON Patients Condition: Leber's Hereditary Optic Neuropathy (LHON) Date: 2016-04-25 Interventions: Drug: Idebenone Raxone 900mg/day as per Raxone SmPC and medical judgement of treating physician. |
Active, not recruiting |
Study Name: A Study Investigating the Safety, Tolerability, and Efficacy of Elamipretide (MTP-131) Topical Ophthalmic Solution for the Treatment of Leber's Hereditary Optic Neuropathy Condition: Leber's Hereditary Optic Neuropathy Date: 2016-02-15 Interventions: Drug: elamipretide (MTP-131) 1% topical ophthalmic solution |
Recruiting |
Study Name: Tracking Neurodegeneration in Early Wolfram Syndrome Condition: Type 1 Diabetes Diabetes Insipidus Diabetes Mellitus Date: 2015-03-05 |