Status | Study |
Enrolling by invitation |
Study Name: A Study to Evaluate Long-term Safety and Clinical Activity of ALN-AS1 in Patient With Acute Intermittent Porphyria (AIP) Condition: Acute Intermittent Porphyria Date: 2016-10-28 Interventions: Drug: ALN-AS1 ALN-AS1 by subcutaneous (SC) injection |
Completed |
Study Name: Assessment of Intra-subject Variability in the Bioavailability of Chlorpromazine Hydrochloride Condition: Anti-Psychotic Management of Manifestations of Psychotic Disorders Date: 2016-10-21 Interventions: Drug: Chlorpromazine Hydrochloride Chlorpromazine Hydrochloride (25 mg Tablet) - Generic US Applicant ho |
Enrolling by invitation |
Study Name: Acute Porphyria Biomarkers Condition: Acute Intermittent Porphyria Hereditary Coproporphyria Date: 2016-10-13 Interventions: Drug: Hemin Hemin will be administered under a separate protocol or for clinical treatment, and samples |
Recruiting |
Study Name: Panhematin for Prevention of Acute Attacks of Porphyria Panhematin for Prevention of Acute Attacks of Porphyria Condition: Acute Intermittent Porphyria Hereditary Coproporphyria Date: 2016-01-01 Interventions: Biological: Hemin for injection |
Recruiting |
Study Name: A Phase 1 Study of ALN-AS1 in Patients With Acute Intermittent Porphyria (AIP) Condition: Acute Intermittent Porphyria Date: 2015-05-19 Interventions: Drug: ALN-AS1 Single or multip |
Recruiting |
Study Name: Controlled Trial of Panhematin in Treatment of Acute Attacks of Porphyria Condition: Acute Porphyrias Date: 2014-06-25 Interventions: Biological: Panhematin Other: Placebo |
Completed |
Study Name: Phase I Gene Therapy Clinical Trial Using the Vector rAAV2/5-PBGD for the Treatment of Acute Intermittent Porphyria Condition: Acute Intermittent Porphyria Date: 2014-02-28 Interventions: Genetic: rAAV2/5-PBGD vector dosage 1 |
Completed |
Study Name: Observational Study of Acute Intermittent Porphyria Patients Condition: Acute Intermittent Porphyria Date: 2014-02-27 |
Not yet recruiting |
Study Name: Dental Health, Diet, Inflammation and Biomarkers in Patients With Acute Intermittent Porphyria(AIP) Condition: Acute Intermittent Porphyria Date: 2012-06-05 |
Recruiting |
Study Name: Clinical Diagnosis of Acute Porphyria Condition: Hereditary Coproporphyria (HCP) Acute Intermittent Porphyria (A Date: 2012-02-16 |