Status | Study |
Not yet recruiting |
Study Name: Harvoni Treatment Porphyria Cutanea Tarda Condition: Porphyria Cutanea Tarda Hepatitis C Date: 2017-04-13 Interventions: Drug: Harvoni One capsule of Harvoni/ ledipasvir, 90 mg + sofosbuvir, 400 mg administered daily for 8, 1 |
Enrolling by invitation |
Study Name: A Study to Evaluate Long-term Safety and Clinical Activity of ALN-AS1 in Patient With Acute Intermittent Porphyria (AIP) Condition: Acute Intermittent Porphyria Date: 2016-10-28 Interventions: Drug: ALN-AS1 ALN-AS1 by subcutaneous (SC) injection |
Enrolling by invitation |
Study Name: Acute Porphyria Biomarkers Condition: Acute Intermittent Porphyria Hereditary Coproporphyria Date: 2016-10-13 Interventions: Drug: Hemin Hemin will be administered under a separate protocol or for clinical treatment, and samples |
Recruiting |
Study Name: Panhematin for Prevention of Acute Attacks of Porphyria Panhematin for Prevention of Acute Attacks of Porphyria Condition: Acute Intermittent Porphyria Hereditary Coproporphyria Date: 2016-01-01 Interventions: Biological: Hemin for injection |
Recruiting |
Study Name: A Phase 1 Study of ALN-AS1 in Patients With Acute Intermittent Porphyria (AIP) Condition: Acute Intermittent Porphyria Date: 2015-05-19 Interventions: Drug: ALN-AS1 Single or multip |
Active, not recruiting |
Study Name: EXPLORE: A Natural History Study of Acute Hepatic Porphyria (AHP) Condition: Acute Hepatic Porphyria Date: 2014-09-11 |
Recruiting |
Study Name: Controlled Trial of Panhematin in Treatment of Acute Attacks of Porphyria Condition: Acute Porphyrias Date: 2014-06-25 Interventions: Biological: Panhematin Other: Placebo |
Completed |
Study Name: Phase I Gene Therapy Clinical Trial Using the Vector rAAV2/5-PBGD for the Treatment of Acute Intermittent Porphyria Condition: Acute Intermittent Porphyria Date: 2014-02-28 Interventions: Genetic: rAAV2/5-PBGD vector dosage 1 |
Completed |
Study Name: Observational Study of Acute Intermittent Porphyria Patients Condition: Acute Intermittent Porphyria Date: 2014-02-27 |
Not yet recruiting |
Study Name: Dental Health, Diet, Inflammation and Biomarkers in Patients With Acute Intermittent Porphyria(AIP) Condition: Acute Intermittent Porphyria Date: 2012-06-05 |