Status | Study |
Enrolling by invitation |
Study Name: Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA Condition: Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) Date: 2013-07-24 Interventions: Drug: scAAVrh74.tMCK.hSGCA |
Completed |
Study Name: Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C Condition: Limb Girdle Muscular Dystrophy Type 2C Gamma-sarcoglycanopathy Date: 2011-03-17 Interventions: Biological: AAV1-gamma-sarcoglycan vector injection single intramuscular injection into carpi radialis m |
Completed |
Study Name: Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) Condition: Muscular Dystrophies Date: 2007-06-27 Interventions: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- First cohort |